Tag Archives: gene

Exclusive: US FDA to ask Sarepta to stop shipments of gene therapy Elevidys, source says – Reuters

Exclusive: US FDA to ask Sarepta to stop shipments of gene therapy Elevidys, source says  Reuters Sarepta shares plunge 40% as future of its gene therapy appears at risk  CNBC FDA to Ask Sarepta to Stop Shipping Muscular Dystrophy Drug Elevidys  The New York Times Third death from a Sarepta gene therapy  BioCentury FDA Is Investigating If Sarepta’s Gene Therapy Should Stay on Market  Bloomberg …

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Sarepta stock falls on FDA gene therapy Elevidys comment

Sarepta stock falls on FDA gene therapy Elevidys comment

Douglas Ingram, president and chief executive officer of Sarepta Therapeutics Inc., during the Forbes Healthcare Summit in New York, US, on Tuesday, Dec. 5, 2023. Michael Nagle | Bloomberg | Getty Images Shares of Sarepta Therapeutics plunged more than 30% on Friday as the future of its approved gene therapy treatment appeared at risk. The Food and Drug Administration will …

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Sarepta Says Another Patient Died After Receiving Gene Therapy – Bloomberg

Sarepta Says Another Patient Died After Receiving Gene Therapy  Bloomberg Patient dies in Sarepta gene therapy trial, adding to safety concerns  STAT Sarepta Therapeutics lays off one-third of workforce in drastic cost-cutting  The Boston Globe Third death from a Sarepta gene therapy  BioCentury Sarepta Therapeutics Stock Is Surging After The Bell: What’s Going On?  Yahoo Finance Source link

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Sarepta to cut 500 jobs, add black-box warning on gene therapy – Reuters

Sarepta to cut 500 jobs, add black-box warning on gene therapy  Reuters Sarepta Therapeutics Announces Strategic Restructuring and Pipeline Prioritization Plan to Maintain Long-term, Sustainable Growth and Provides Update on ELEVIDYS Label  Sarepta Therapeutics Sarepta Soars as Gene Therapy Stays on Market With Warning  Bloomberg Sarepta pivots to siRNA and lays off 500 staffers as Elevidys gets box warning  Fierce Biotech Sarepta Therapeutics Halts …

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Sarepta Soars as Gene Therapy Stays on Market With Warning – Bloomberg

Sarepta Soars as Gene Therapy Stays on Market With Warning  Bloomberg Sarepta Therapeutics Announces Strategic Restructuring and Pipeline Prioritization Plan to Maintain Long-term, Sustainable Growth and Provides Update on ELEVIDYS Label  Sarepta Therapeutics Sarepta pivots to siRNA and lays off 500 staffers as Elevidys gets box warning  Fierce Biotech Sarepta Therapeutics Halts ELEVIDYS Shipments for Non-Ambulatory DMD Patients  Yahoo Finance Sarepta Therapeutics lays off …

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Gene Key to MS Immune Regulation Discovered

Gene Key to MS Immune Regulation Discovered

Summary: New research has identified the gene Egr-1 as a critical regulator of immune balance, offering hope for autoimmune disease therapies. In a mouse model of multiple sclerosis, loss of Egr-1 led to reduced regulatory T cell activity and heightened inflammation. The study showed Egr-1 directly boosts the expression of Foxp3, a protein essential for Treg cells, via the TGF-β …

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In a first, congenital deafness in teens and adults treated with new gene therapy

In a first, congenital deafness in teens and adults treated with new gene therapy

Up to 3 in every 1,000 newborns has hearing loss in one or both ears. While cochlear implants offer remarkable hope for these children, it requires invasive surgery. These implants also cannot fully replicate the nuance of natural hearing. But recent research my colleagues and I conducted has shown that a form of gene therapy can successfully restore hearing in …

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